Experimental treatment for Niemann-Pick disease appears safe
Por um escritor misterioso
Descrição
An experimental drug has appeared to slow the progression of Niemann-Pick disease the drug 2-hydroxypropyl-beta-cyclodextrin is being tested
TRIALS: A Fight for Children with Niemann-Pick Type C, a Fatal Genetic Disease
IJMS, Free Full-Text
Frontiers Pre-clinical Mouse Models of Neurodegenerative Lysosomal Storage Diseases
Niemann–Pick type C disease: cellular pathology and pharmacotherapy - Wheeler - 2020 - Journal of Neurochemistry - Wiley Online Library
Full article: Current advancements in therapy for Niemann-Pick disease: progress and pitfalls
FDA needs to be more flexible assessing rare disease treatments - STAT
Experimental treatment for Niemann-Pick disease type C1 appears safe, effective
Niemann Pick Disease Type C - Symptoms, Causes, Treatment
Niemann-Pick Disease, Type B disease: Malacards - Research Articles, Drugs, Genes, Clinical Trials
TPC2 rescues lysosomal storage in mucolipidosis type IV, Niemann–Pick type C1, and Batten disease
Current advancements in therapy for Niemann-Pick disease: progress and pitfalls: Expert Opinion on Pharmacotherapy: Vol 24, No 11
de
por adulto (o preço varia de acordo com o tamanho do grupo)
